raav2 Search Results


aav2 cas9  (PackGene Biotech lnc)
95
PackGene Biotech lnc aav2 cas9
Aav2 Cas9, supplied by PackGene Biotech lnc, used in various techniques. Bioz Stars score: 95/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc12930510-150-8-14?v=PackGene+Biotech+lnc
Average 95 stars, based on 1 article reviews
aav2 cas9 - by Bioz Stars, 2026-07
95/100 stars
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raav2  (Genechem)
86
Genechem raav2
Raav2, supplied by Genechem, used in various techniques. Bioz Stars score: 86/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/10__1172_slash_jci196944-282-15-24?v=Genechem
Average 86 stars, based on 1 article reviews
raav2 - by Bioz Stars, 2026-07
86/100 stars
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aav retro  (Addgene inc)
94
Addgene inc aav retro
Aav Retro, supplied by Addgene inc, used in various techniques. Bioz Stars score: 94/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/baughn_michael_welton__2021__therapeutic_restoration_of_stathmin_2_rna_processing_in_tdp_43_proteinopathies-963-23-24?v=Addgene+inc
Average 94 stars, based on 1 article reviews
aav retro - by Bioz Stars, 2026-07
94/100 stars
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virus raav2  (Addgene inc)
94
Addgene inc virus raav2
Virus Raav2, supplied by Addgene inc, used in various techniques. Bioz Stars score: 94/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc10203190-30-4-10?v=Addgene+inc
Average 94 stars, based on 1 article reviews
virus raav2 - by Bioz Stars, 2026-07
94/100 stars
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raav2-cb-hrpe65  (Applied Genetic Technologies Corporation)
90
Applied Genetic Technologies Corporation raav2-cb-hrpe65
Raav2 Cb Hrpe65, supplied by Applied Genetic Technologies Corporation, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc07701157-63-9-11?v=Applied+Genetic+Technologies+Corporation
Average 90 stars, based on 1 article reviews
raav2-cb-hrpe65 - by Bioz Stars, 2026-07
90/100 stars
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β-galactosidase assay raav-2-lacz  (Promega)
90
Promega β-galactosidase assay raav-2-lacz
β Galactosidase Assay Raav 2 Lacz, supplied by Promega, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc01606626-35-9-44?v=Promega
Average 90 stars, based on 1 article reviews
β-galactosidase assay raav-2-lacz - by Bioz Stars, 2026-07
90/100 stars
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raav2-colq-myc  (VectorBuilder GmbH)
90
VectorBuilder GmbH raav2-colq-myc
Raav2 Colq Myc, supplied by VectorBuilder GmbH, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pm37356721-337-40-55?v=VectorBuilder+GmbH
Average 90 stars, based on 1 article reviews
raav2-colq-myc - by Bioz Stars, 2026-07
90/100 stars
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raav2-retro  (Albaugh LLC)
90
Albaugh LLC raav2-retro
Raav2 Retro, supplied by Albaugh LLC, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc09559170-45-2-21?v=Albaugh+LLC
Average 90 stars, based on 1 article reviews
raav2-retro - by Bioz Stars, 2026-07
90/100 stars
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raav2/5-hnaglu  (uniQure Inc)
90
uniQure Inc raav2/5-hnaglu
Overview of approved, orphan drug designations, off-labeled therapies for treating lysosomal storage disorders, and examples of some products under development with an orphan drug designation.
Raav2/5 Hnaglu, supplied by uniQure Inc, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc07693645-58-1-2?v=uniQure+Inc
Average 90 stars, based on 1 article reviews
raav2/5-hnaglu - by Bioz Stars, 2026-07
90/100 stars
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raav2/9-cag-nir-fps-p2a-egfp viruses  (SunBio Inc)
90
SunBio Inc raav2/9-cag-nir-fps-p2a-egfp viruses
Overview of approved, orphan drug designations, off-labeled therapies for treating lysosomal storage disorders, and examples of some products under development with an orphan drug designation.
Raav2/9 Cag Nir Fps P2a Egfp Viruses, supplied by SunBio Inc, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pm37666982-467-31-34?v=SunBio+Inc
Average 90 stars, based on 1 article reviews
raav2/9-cag-nir-fps-p2a-egfp viruses - by Bioz Stars, 2026-07
90/100 stars
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raav2-zsgreen-shrna-scramble  (Biowit Technologies)
90
Biowit Technologies raav2-zsgreen-shrna-scramble
Overview of approved, orphan drug designations, off-labeled therapies for treating lysosomal storage disorders, and examples of some products under development with an orphan drug designation.
Raav2 Zsgreen Shrna Scramble, supplied by Biowit Technologies, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc05802212-36-13-21?v=Biowit+Technologies
Average 90 stars, based on 1 article reviews
raav2-zsgreen-shrna-scramble - by Bioz Stars, 2026-07
90/100 stars
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subretinal tgaag76 (raav 2/2.hrpe65p.hrpe65)  (Targeted Genetics Corporation)
90
Targeted Genetics Corporation subretinal tgaag76 (raav 2/2.hrpe65p.hrpe65)
Clinical trials of gene therapy using viral vectors for IRDs ( ClinicalTrials.gov ).
Subretinal Tgaag76 (Raav 2/2.Hrpe65p.Hrpe65), supplied by Targeted Genetics Corporation, used in various techniques. Bioz Stars score: 90/100, based on 1 PubMed citations. ZERO BIAS - scores, article reviews, protocol conditions and more
https://www.bioz.com/product/raav2/pmc09334564-9-6-26?v=Targeted+Genetics+Corporation
Average 90 stars, based on 1 article reviews
subretinal tgaag76 (raav 2/2.hrpe65p.hrpe65) - by Bioz Stars, 2026-07
90/100 stars
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Image Search Results


Overview of approved, orphan drug designations, off-labeled therapies for treating lysosomal storage disorders, and examples of some products under development with an orphan drug designation.

Journal: Frontiers in Molecular Biosciences

Article Title: CNS-Targeting Therapies for Lysosomal Storage Diseases: Current Advances and Challenges

doi: 10.3389/fmolb.2020.559804

Figure Lengend Snippet: Overview of approved, orphan drug designations, off-labeled therapies for treating lysosomal storage disorders, and examples of some products under development with an orphan drug designation.

Article Snippet: , rAAV2/5-hNAGLU (UniQure Biopharma B.V.) , IT-GT (local) rAAV2/5-hNAGLU , No results from clinical trials NCT03300453.

Techniques: Produced, Ex Vivo, Modification, Recombinant

Clinical trials of gene therapy using viral vectors for IRDs ( ClinicalTrials.gov ).

Journal: Frontiers in Medicine

Article Title: Advancing precision medicines for ocular disorders: Diagnostic genomics to tailored therapies

doi: 10.3389/fmed.2022.906482

Figure Lengend Snippet: Clinical trials of gene therapy using viral vectors for IRDs ( ClinicalTrials.gov ).

Article Snippet: 1/2 , LCA , RPE65 , Subretinal tgAAG76 (rAAV 2/2.hRPE65p.hRPE65) , Moderate and temporary improvement of retinal sensitivity , National Institute for Health Research and others; Targeted Genetics Corporation , NCT00643747.

Techniques: Clinical Proteomics, Plasmid Preparation, Injection, Functional Assay