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Cholestech Corporation
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BioIVT Inc
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Lipid Analytical Laboratories
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BASF
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CJ Cheiljedang Corporation
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Siemens AG
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Fonterra Co operative Group Limited
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OXIS International
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Becton Dickinson
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ANSES laboratories
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Northwest Lipid Research Laboratories
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Skylight Biotech Inc
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Image Search Results
Journal: Nucleic Acids Research
Article Title: Conjugation of hydrophobic moieties enhances potency of antisense oligonucleotides in the muscle of rodents and non-human primates
doi: 10.1093/nar/gkz360
Figure Lengend Snippet: Conjugation of hydrophobic moieties to PS ASOs modulates plasma protein binding and enhances activity in extra-hepatic tissues. ( A ) Binding curves and ( B ) dissociation constants of palmitate, tocopherol and cholesterol ASOs with albumin, HDL, LDL and HRG. NB = no binding ( C ) Structures of hydrophobic moieties conjugated to PS ASOs. Palm = palmitic acid, Toc = tocopherol, Chol = cholesterol, Blue = cEt and black = DNA nucleotides. ( D ) Comparison of protein binding profiles of palmitate, tocopherol and cholesterol conjugated PS ASOs in mouse, rat, monkey and human plasma by size exclusion chromatography. (E) All ASOs showed similar activity in 3T3-L1 cells for reducing MALAT-1 RNA when delivered by free uptake. ( F ) Conjugation of hydrophobic moieties enhances potency of a PS ASO gapmer targeting MALAT-1 RNA in the liver and heart. All errors are ±std. dev.
Article Snippet: Plasma from human, mouse, rat or monkey (
Techniques: Conjugation Assay, Protein Binding, Activity Assay, Binding Assay, Size-exclusion Chromatography